US Researchers have used ‘Prime Editing’, a cutting-edge gene-editing technique, to treat a person for the first time. The recipient is a teenager with a rare immune disorder.
https://www.nature.com/articles/d41586-025-01593-z?
US Researchers have used ‘Prime Editing’, a cutting-edge gene-editing technique, to treat a person for the first time. The recipient is a teenager with a rare immune disorder.
https://www.nature.com/articles/d41586-025-01593-z?
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Submission Statement
*“Researchers designed the treatment to correct a mutation that causes chronic granulomatous disease, a dangerous condition that disables a variety of immune cells, including those called neutrophils. A month after the teenager received the treatment, he had experienced no serious side effects. And the therapy seemed to have restored the function of a crucial enzyme in two-thirds of his neutrophils — more than enough to provide a significant boost to his immune system.”*
According to the researchers, prime editing is an upgrade to the CRISPR-Cas9 treatments. It’s still too early to tell if this change will be permanent, but these early signs are gratifying.
How long until we hear something like this for cancer!? How can we cure these rare diseases with little study and still can’t do anything more than chemo for 99% of the population?